addressing treatment challenges in cystic fibrosis
DESCRIPTION
Addressing Treatment Challenges in Cystic Fibrosis. Program Goals. Pseudomonas aeruginosa. Eradication of Mucoid Pseudomonas Infection EPIC Clinical Trial*. EPIC Results. Management of Exacerbations. Cystic Fibrosis Guidelines. Cystic Fibrosis Guidelines. - PowerPoint PPT PresentationTRANSCRIPT
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Addressing Treatment Challenges in Cystic Fibrosis
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Program Goals
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Pseudomonas aeruginosa
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Eradication of Mucoid Pseudomonas Infection
EPIC Clinical Trial*
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EPIC Results
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Management of Exacerbations
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Cystic Fibrosis Guidelines
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Cystic Fibrosis Guidelines
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Why Don’t Physicians FollowClinical Practice Guidelines?
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Personalized Medicine Targeting the CFTR
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Strategies for Modifying the Underlying Defect in CF
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Strategies for Modifying the Underlying Defect in CF (cont)
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Ivacaftor in Patients With CF and the G551D Mutation
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F508 (F508del)
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Corrector TherapyPhase 2 Results of Lumacaftor + Ivacaftor
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Looking to the Future
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Will Improving CFTR Function Affect Chronic Pseudomonas
Infection?
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Practical Advice to Address the Challenges of Complex Medical
Regimens
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Abbreviations
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References
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References (cont)
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References (cont)
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References (cont)