orphan drugs in emerging markets
DESCRIPTION
Market access issues for orphan drugs in Emerging MarketsTRANSCRIPT
PARIOFORMA
An international pharmaceutical company commissioned Parioforma to investigate
learnings from recent reimbursement applications for Orphan Drugs in selected
Emerging Markets.
Client objectives
◦ Gain a better understanding of the treatment environment for orphan diseases in selected
Emerging Markets:
Funding mechanisms
Unmet needs
Current clinical practice and access to care
◦ Gain a better understanding of the Evidence requirements to support the reimbursement of
Orphan Drugs in these countries:
Assessment of the importance of trial parameters on the decision to reimburse
Assessment of the importance of clinical parameters on the decision to reimburse
◦ Identify informal practices different to the formal policy described in Government documents
◦ Identify reasons for the non-reimbursement of certain Orphan therapies in recent years
Programme of work
◦ Desk research was used to gain an overview into formal Government published procedures
regarding patient access to and the funding of Orphan Drugs
◦ Interviews were conducted with payers and KOLs to confirm and validate official requirements
and procedures for the reimbursement of such drugs as well as to gain a more balanced view on
official procedures vs. informal practices and the reasons behind recent unsuccessful
reimbursement applications
◦ Available evidence was assessed and a report was prepared covering the detailed findings, with
key recommendations for the client
Value
◦ The results of the project allowed the client to gain a clear understanding of the parameters that
influence access to funding of Orphan Drugs in these markets, enabling them to adapt their global
market access strategy for a better fit to emerging markets
For further information, or to discuss your market access, pricing and
reimbursement intelligence requirements, contact US now…
Parioforma Ltd – 55 Prices Gate – Exhibition Road –
London SW7 2PN – United Kingdom
www.parioforma.com
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