introduction to decision analytic modelling · 2019-04-05 · modeling approaches •technique...

31
1 CAPHRI School for Public Health and Primary Care Introduction to decision analytic modelling Prof. Dr. Manuela Joore Dept. Clinical Epidemiology & MTA, Maastricht UMC+, [email protected] EUHEA pre-conference workshop July 11th 2018

Upload: others

Post on 10-Aug-2020

3 views

Category:

Documents


0 download

TRANSCRIPT

Page 1: Introduction to decision analytic modelling · 2019-04-05 · Modeling approaches •Technique should match conceptual model –Decision tree •No explicit modeling of time, easy/messy

1

CAPHRI School for Public Health and Primary Care

Introduction to decision analytic modelling

Prof. Dr. Manuela Joore Dept. Clinical Epidemiology & MTA, Maastricht UMC+, [email protected]

EUHEA pre-conference workshop July 11th 2018

Page 2: Introduction to decision analytic modelling · 2019-04-05 · Modeling approaches •Technique should match conceptual model –Decision tree •No explicit modeling of time, easy/messy

2

CAPHRI School for Public Health and Primary Care

Outline • Decision analytic modelling for health

economic evaluation: – What is it & why use it?

– Types/Approaches

– Components

– Analyses

Page 3: Introduction to decision analytic modelling · 2019-04-05 · Modeling approaches •Technique should match conceptual model –Decision tree •No explicit modeling of time, easy/messy

3

CAPHRI School for Public Health and Primary Care

What is a decision analytic model? (for health economic evaluation)

Page 4: Introduction to decision analytic modelling · 2019-04-05 · Modeling approaches •Technique should match conceptual model –Decision tree •No explicit modeling of time, easy/messy

4

CAPHRI School for Public Health and Primary Care

What is a definition of ‘model’?

Page 5: Introduction to decision analytic modelling · 2019-04-05 · Modeling approaches •Technique should match conceptual model –Decision tree •No explicit modeling of time, easy/messy

5

CAPHRI School for Public Health and Primary Care

What is a definition of ‘model’?

A model is a simplified reflection

of reality

Page 6: Introduction to decision analytic modelling · 2019-04-05 · Modeling approaches •Technique should match conceptual model –Decision tree •No explicit modeling of time, easy/messy

6

CAPHRI School for Public Health and Primary Care

Can you think of examples of models?

Page 7: Introduction to decision analytic modelling · 2019-04-05 · Modeling approaches •Technique should match conceptual model –Decision tree •No explicit modeling of time, easy/messy

7

CAPHRI School for Public Health and Primary Care

Page 8: Introduction to decision analytic modelling · 2019-04-05 · Modeling approaches •Technique should match conceptual model –Decision tree •No explicit modeling of time, easy/messy

8

CAPHRI School for Public Health and Primary Care Δ

Δ QALYs

Health economic evaluation: two approaches

Page 9: Introduction to decision analytic modelling · 2019-04-05 · Modeling approaches •Technique should match conceptual model –Decision tree •No explicit modeling of time, easy/messy

9

CAPHRI School for Public Health and Primary Care Δ

Δ QALYs

Health economic evaluation: two approaches

R R

Intervention A

Intervention B

€, QALYs

€, QALYs

Mo

de

l Tri

al

Mild Severe

Death

Page 10: Introduction to decision analytic modelling · 2019-04-05 · Modeling approaches •Technique should match conceptual model –Decision tree •No explicit modeling of time, easy/messy

10

CAPHRI School for Public Health and Primary Care

Why model?

Page 11: Introduction to decision analytic modelling · 2019-04-05 · Modeling approaches •Technique should match conceptual model –Decision tree •No explicit modeling of time, easy/messy

11

CAPHRI School for Public Health and Primary Care

Policy decisions

Scientific knowledge

Health economic decision modelling

RCTs, cohort studies / registries, surveys, hospital information, price information, expert opinion...

Is A cost-effective compared to B (C, D, …)

Page 12: Introduction to decision analytic modelling · 2019-04-05 · Modeling approaches •Technique should match conceptual model –Decision tree •No explicit modeling of time, easy/messy

12

CAPHRI School for Public Health and Primary Care

Model based economic evaluation: Why?

1. Extending results from a trial = extrapolation

2. Combining / synthesizing available evidence

3. Generalising trials into practice (location, population, …)

4. Modelling prior to trials and studies

5. Modelling to address uncertainty

population S

?

Page 13: Introduction to decision analytic modelling · 2019-04-05 · Modeling approaches •Technique should match conceptual model –Decision tree •No explicit modeling of time, easy/messy

13

CAPHRI School for Public Health and Primary Care

Components in modelling

Page 14: Introduction to decision analytic modelling · 2019-04-05 · Modeling approaches •Technique should match conceptual model –Decision tree •No explicit modeling of time, easy/messy

14

CAPHRI School for Public Health and Primary Care

Components in modelling (see ISPOR/SMDM taskforce papers, Value in Health 2012 vol 15: p 796 etc.)

1. Conceptualising a model

2. Specific modeling techniques

3. Parametrizing a model

4. Handling uncertainty

5. Model validation & transparency

Page 15: Introduction to decision analytic modelling · 2019-04-05 · Modeling approaches •Technique should match conceptual model –Decision tree •No explicit modeling of time, easy/messy

15

CAPHRI School for Public Health and Primary Care

1. Conceptualising a model (ISPOR/SMDMD taskforce 2)

Page 16: Introduction to decision analytic modelling · 2019-04-05 · Modeling approaches •Technique should match conceptual model –Decision tree •No explicit modeling of time, easy/messy

16

CAPHRI School for Public Health and Primary Care

1. Conceptualising a model

1. Model should match the decision, not vice versa

2. Specify the decision problem

– population, intervention, comparators, outcomes, time horizon, perspective, audience)

3. Conceptual structure of the model driven by decision problem not by data availability

4. Conceptual model should be able to indentify key uncertainties

Page 17: Introduction to decision analytic modelling · 2019-04-05 · Modeling approaches •Technique should match conceptual model –Decision tree •No explicit modeling of time, easy/messy

17

CAPHRI School for Public Health and Primary Care

Components in modelling (see ISPOR/SMDM taskforce papers, Value in Health 2012 vol 15: p 796 etc.)

1. Conceptualising a model

2. Specific modeling techniques

3. Parametrizing a model

4. Handling uncertainty

5. Model validation & transparency

Page 18: Introduction to decision analytic modelling · 2019-04-05 · Modeling approaches •Technique should match conceptual model –Decision tree •No explicit modeling of time, easy/messy

18

CAPHRI School for Public Health and Primary Care

Modeling approaches

Page 19: Introduction to decision analytic modelling · 2019-04-05 · Modeling approaches •Technique should match conceptual model –Decision tree •No explicit modeling of time, easy/messy

19

CAPHRI School for Public Health and Primary Care

Modeling approaches

• Technique should match conceptual model

– Decision tree • No explicit modeling of time, easy/messy

– State transition model • Widely used

– Discrete event simulation • Constrained resources / interaction between individuals / time-

to-event data / need to record individual experience

– Dynamic transmission model • Infectious disease

Page 20: Introduction to decision analytic modelling · 2019-04-05 · Modeling approaches •Technique should match conceptual model –Decision tree •No explicit modeling of time, easy/messy

20

CAPHRI School for Public Health and Primary Care

Decision tree

Option A

Option B

Healthy

Disease

Death

Healthy

Disease

Death

Healthy

Disease

Death

IDEM

0.6

0.1

0.3

Etc.

Etc.

Etc.

Etc.

Page 21: Introduction to decision analytic modelling · 2019-04-05 · Modeling approaches •Technique should match conceptual model –Decision tree •No explicit modeling of time, easy/messy

21

CAPHRI School for Public Health and Primary Care

State transition model (ISPOR/SMDM taskforce 3)

• Conceptualizes a decision problem in terms of – mutually exclusive and collectively exhaustive health states

– transitions among those states

Page 22: Introduction to decision analytic modelling · 2019-04-05 · Modeling approaches •Technique should match conceptual model –Decision tree •No explicit modeling of time, easy/messy

22

CAPHRI School for Public Health and Primary Care

State transition model: mutually exclusive & collectively exhaustive health states & transitions between those states

• Health states

• Transitions

• Utilities & Costs

– Health states

– Transitions

Alive

Death

Page 23: Introduction to decision analytic modelling · 2019-04-05 · Modeling approaches •Technique should match conceptual model –Decision tree •No explicit modeling of time, easy/messy

23

CAPHRI School for Public Health and Primary Care

State transition model: mutually exclusive & exhaustive health states

• Population with disease X, mild stage

• Patients may progress to severe and have increased mortality risk, but may also improve

• New treatment may decrease probability of progression and mortality

• Can you think of a model structure?

Page 24: Introduction to decision analytic modelling · 2019-04-05 · Modeling approaches •Technique should match conceptual model –Decision tree •No explicit modeling of time, easy/messy

24

CAPHRI School for Public Health and Primary Care

State transition model: mutually exclusive & exhaustive health states

Healthy Disease

Death

Page 25: Introduction to decision analytic modelling · 2019-04-05 · Modeling approaches •Technique should match conceptual model –Decision tree •No explicit modeling of time, easy/messy

25

CAPHRI School for Public Health and Primary Care

State transition model: comparing health care technologies

Healthy Disease

Death

Healthy Disease

Death

Page 26: Introduction to decision analytic modelling · 2019-04-05 · Modeling approaches •Technique should match conceptual model –Decision tree •No explicit modeling of time, easy/messy

26

CAPHRI School for Public Health and Primary Care

State transition model: Timing - discrete

Healthy Disease

Death

Healthy Disease

Death

Healthy Disease

Death

Cycle 0

Cycle 1

Cycle 2

Etcetera Time horizon

Page 27: Introduction to decision analytic modelling · 2019-04-05 · Modeling approaches •Technique should match conceptual model –Decision tree •No explicit modeling of time, easy/messy

27

CAPHRI School for Public Health and Primary Care

State transition model (ISPOR/SMDM taskforce 3)

• Conceptualizes a decision problem in terms of – mutually exclusive and collectively exhaustive health states

– transitions among those states

• Takes timing into account

• Suitable to model the dynamics of disease and intervention (recurrent events)

• Markovian property (hence “Markov model”) – transition probabilities do not depend on history neither on past

states nor on the time spent in the current state

– very limiting!

Page 28: Introduction to decision analytic modelling · 2019-04-05 · Modeling approaches •Technique should match conceptual model –Decision tree •No explicit modeling of time, easy/messy

28

CAPHRI School for Public Health and Primary Care

Training 1 – conceptualising a model

• 20 minutes!

Page 29: Introduction to decision analytic modelling · 2019-04-05 · Modeling approaches •Technique should match conceptual model –Decision tree •No explicit modeling of time, easy/messy

29

CAPHRI School for Public Health and Primary Care

Manuela Joore

Professor HTA & Decision Making Deputy Head Department Clinical Epidemiology & Medical Technology Assessment

Maastricht University Hospital PO Box 5800

6202 AZ The Netherlands [email protected]

Page 30: Introduction to decision analytic modelling · 2019-04-05 · Modeling approaches •Technique should match conceptual model –Decision tree •No explicit modeling of time, easy/messy

30

CAPHRI School for Public Health and Primary Care

State transition model: mutually exclusive & exhaustive health states

Healthy Disease

Death

Page 31: Introduction to decision analytic modelling · 2019-04-05 · Modeling approaches •Technique should match conceptual model –Decision tree •No explicit modeling of time, easy/messy

31

CAPHRI School for Public Health and Primary Care

Training 1

• Time horizon:

• Modelling approach:

• Structure:

• What types of information do you need?