29 12 5 () 10:0017:20
29 12 6 () 9:0016:10




- 1 -
1 29 12 5
10:0010:10 Session 1 10:1011:00
1.
11:0011:05
Session microRNA 11:0512:35 /
2.
3.
1,2, 3, 2, 2, 4, 1,5, 6, 2
1 , 2 , 3
, 4 , 5 , 6
4.
miRNA 1, 1, 2, 2
1 , 2
- 2 -
Smpd3 mdx
1, 2, 1, 3, 4, 4, 5,
5, 6, 6, 6
1 , 2
, 3 , 4
, 5, 6
6. (Unloading)
1, 1, 1, 1, 2, 3, 3, 4
1 , 2 , 3
, 4
12:3513:45
7. -
——
, ,
8.

9
1, 1, 1, 2, 3, 3
1 , 2 , 3

15:3015:50
Session iPS 15:5017:20 12.

1, 1, 2, 3, 3, 4, 5, 6
1 , 2 3 , 4
, 5 , 6
- 4 -
13.

1, 1,2, 1, 1, 1, 2
1, 2
14. iPS 1, 1, 1, 1, 1, 1, 1, 1
2, 3
1 iPS , 2, 3
15. ES
1, 2, 1, 1
1, 2
16.

- 5 -
2 29 12 6 ()
Session 9:0010:20
17.
1,2, Tirsa LE van Westering2, Henrik J Johansson3, 1, 1, Janne Lehtiö3, 4,
Matthew JA Wood2, Thomas C Roberts2,5, 1
1Dept of Molecular Therapy, National Center of Neurology and Psychiatry (NCNP), Japan, 2 Dept of Physiology,
Anatomy and Genetics, University of Oxford, UK, 3 Dept of Oncology/Pathology, Cancer proteomics Mass Spectr
ometry, Karolinska Institutet, Sweden, 4 Dept of Medical Genetics, School of Human Development, University of
Alberta, Canada, 5 Sanford Burnham Prebys Medical Discovery Institute, USA
18.
2’- 1, 1, 2, 2, 2, 2, 2, 3
4, 5
1 , 2, 3 , 4
, 5
19. ENA DS-5141b 1, 2
1 , 2 LCM 2G
20. FSHD)
1, Ashley Guncay1, Kenji RQ Lim1, 1, Yi-Wen Chen2
1 University of Alberta, Faculty of Medicine and Dentistry, 2 Children’s National Health Systems (Washington DC)
- 6 -
DMD 1, Emma Tabe Eko Niba2
1 , 2
Session 2 10:3011:30
22. Integration of biomarkers into clinical trials for DMD
Eric Hoffman Binghamton University
11:3012:45
Session 12:4513:30 23. DMD
AAV DMD 1,2, 1,2,3, 1,2,3, 3, 2,3, 4, 4, 3
1 , 2 , 3
, 4 JCR
24.

26.
1, 1, 2, 3
1 , 2 , 3
27.
1 , 2 28.
G-CSF DMD 1, 1, 2, 2
1 , 2
14:2514:45
29. Simple Western dystrophin
,

30. Dp116 DMD
1, 2, 3, 3, 3
1 , 2 , 3,

Session 15:2516:10
31. , , , , , , ,

32.
1, 1, 1,2, 3, 3, 1,4, 5, 1
1,6
, 3 , 4
, 5 , 6
- 9 -
33.

, , , , , , , ,
,
- 10 -
11
12

29 12 5 () 10:0017:20